"Last week, the Food and Drug Administration issued an announcement with a title only a federal bureaucrat could write: “FDA approves Kalydeco to treat rare form of cystic fibrosis.’’ In fact, it was a blockbuster development, the first drug that would treat the cause, rather than the symptoms, of cystic fibrosis, a medication that showed such breathtaking results in clinical trials that it was sanctioned by the FDA in about half the typical time.Behind that announcement sits a human narrative, a quarter century in the making, of loss, hope, and triumph."
Driven by loss, father inspires tireless pursuit of a cure
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Planet of the Blind 